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Paper Title
Genetic therapy in a mitochondrial disease model suggests a critical role for liver dysfunction in mortality.
PubMed
Paper Journal Title
eLife
Paper Citation Count
2
Paper Publication Year
2022
Bio Mention
LSFC, Leigh Syndrome, dysfunction in lipid homeostasis, liver dysfunction, mitochondrial disease, mitochondrial disorder, mitochondrial disorders, mitochondrial mRNA, patients, protein-coding genes, zebrafish
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Author Name
Affiliation
Stephen C Ekker
Mayo Clinic College of Medicine
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