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Paper Details

Genetic therapy in a mitochondrial disease model suggests a critical role for liver dysfunction in mortality.
eLife
2
2022
LSFC, Leigh Syndrome, dysfunction in lipid homeostasis, liver dysfunction, mitochondrial disease, mitochondrial disorder, mitochondrial disorders, mitochondrial mRNA, patients, protein-coding genes, zebrafish
Author NameAffiliation
Stephen C EkkerMayo Clinic College of Medicine
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