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Paper Details
Paper Title
Gene Therapy for Spinal Muscular Atrophy: Safety and Early Outcomes.
PubMed
Paper Journal Title
Pediatrics
Paper Citation Count
69
Paper Publication Year
2020
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Author Name
Affiliation
Garey Noritz
Nationwide Children's Hospital and The Ohio State University
Eileen Broomall
Cincinnati Children's Hospital
Nancy Bass
Rainbow Babies and Children's Hospital
1 - 3
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