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Paper Details

Strategies for Treating Inherited Retinal Degeneration With Large Genes That Are Not Amenable to Adeno-Associated Virus-Based Gene Replacement Therapy.
JAMA Ophthalmol
0
2021
Author NameAffiliation
Mark E PennesiCasey Eye Institute, Oregon Health and Science University
Mark E PennesiOregon Health and Science University
Mark E PennesiOregon Health and Science University
Richard G WeleberCasey Eye Institute, Oregon Health and Science University
Richard G WeleberOregon Health and Science University
Richard G WeleberOregon Health and Science University
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