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Paper Details

A targeted antisense therapeutic approach for Hutchinson-Gilford progeria syndrome.
Nat Med
43
2021
HGPS, Hutchinson-Gilford progeria syndrome, LMNA gene, SRP, SRP-2001, accelerated aging disorder, human, lamin A, mouse, mutant transcripts, myocardial infarction, patient, phosphorodiamidate morpholino, premature death, progerin, progerin transcripts, stroke, vascular smooth muscle cell
Author NameAffiliation
Michael R ErdosNational Human Genome Research Institute, National Institutes of Health
Michael R ErdosNational Human Genome Research Institute, National Institutes of Health
Narisu NarisuNational Human Genome Research Institute, National Institutes of Health
Francis S CollinsNational Human Genome Research Institute, National Institutes of Health
Francis S CollinsNational Human Genome Research Institute, National Institutes of Health
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