Skip to Main Content

Paper Details

Preventing formation of toxic N-terminal huntingtin fragments through antisense oligonucleotide-mediated protein modification.
Nucleic Acid Ther
41
2014
586, 586 amino acid N, 586 amino acid N-terminal huntingtin fragments, HD, HTT, HTT gene, Huntington's disease, N, N-terminal huntingtin fragments, amino acid, autosomal dominant disorder, exon 12, full, huntingtin, huntingtin pre-mRNA, huntingtin protein, mouse, mutant huntingtin, neurodegeneration, polyglutamine

Datasets