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Paper Details

Editing outside the body: Ex vivo gene-modification for β-hemoglobinopathy cellular therapy.
Molecular Therapy
8
2021
-thalassemia, gene-modified cells, hematopoietic, hematopoietic stem cell, hematopoietic stem cell genomes, hemoglobinopathies, hemoglobinopathy, human, monogenic disorders, patient, sickle cell disease, somatic cells, stem cells
Author NameAffiliation
Daniel E BauerHarvard Medical School, Boston Children's Hospital, Dana-Farber Cancer Institute, USA Harvard Stem Cell Institute, USA Broad Institute
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