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Paper Details

Characterization of the humanized FRG mouse model and development of an AAV-LK03 variant with improved liver lobular biodistribution.
Mol Ther Methods Clin Dev
5
2023
FRG, HSPG, genetic diseases, human, human hepatocytes, humanized, liver xenograft, mice, mouse, primary hepatocytes, sn-RNA
Author NameAffiliation
Alistair R R ForrestHarry Perkins Institute of Medical Research, QEII Medical Centre and Centre for Medical Research, The University of Western Australia
Alistair R R ForrestHarry Perkins Institute of Medical Research, QEII Medical Centre and Centre for Medical Research, The University of Western Australia
Leszek LisowskiTranslational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney
Leszek LisowskiMilitary Institute of Medicine
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