Skip to Main Content

Paper Details

Natural gene therapy in monozygotic twins with Fanconi anemia.
Blood
64
2006
2555deltaT, 2670G, 2927G, A, E966K, FA, FANCA gene, Fanconi anemia, HSC, R880Q, Skin fibroblasts, committed hematopoietic progenitors, exon 27, exon 30, fibroblasts, functionally corrected HSC, hematopoietic cells, hematopoietic stem cell, hematopoietic stem cells, lymphocytes, maternal exon 28, mutant FANCA (R880Q), patients, skin cells

Datasets