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Paper Details

Continued benefit of nusinersen initiated in the presymptomatic stage of spinal muscular atrophy: 5-year update of the NURTURE study.
Muscle Nerve
17
2023
Children, SMA, SMN2, SMN2 copies, areflexia, child, children, nusinersen, spinal muscular atrophy
Author NameAffiliation
Kathryn J SwobodaCenter for Genomic Medicine, Massachusetts General Hospital
Enrico BertiniPost-Graduate Bambino Gesu Children's Research Hospital, IRCCS
Enrico BertiniPost-Graduate Bambino Gesu Children's Research Hospital, IRCCS
Richard S FinkelCenter for Experimental Neurotherapeutics, St. Jude Children's Research Hospital
Richard S FinkelNemours Children's Hospital
Nancy L KuntzAnn & Robert H. Lurie Children's Hospital of Chicago
Tawfeg Ben-Omran
Tawfeg Ben-OmranHamad Medical Corporation
Richard Foster
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Release 1.2