Skip to Main Content

Paper Details

Biodistribution of onasemnogene abeparvovec DNA, mRNA and SMN protein in human tissue.
Nat Med
47
2021
Author NameAffiliation
Petra KaufmannNovartis Gene Therapies
Wendy K ChungColumbia University
Wendy K ChungColumbia University
Robert F HevnerUniversity of California
Christopher R PiersonNationwide Children's Hospital
Christopher R PiersonThe Ohio State University
Francesco MuntoniNational Institute for Health Research, Great Ormond Street Institute of Child Health Biomedical Research Centre, University College London
Francesco MuntoniGreat Ormond Street Hospital Trust
  • 1 - 8

Datasets

Release 1.2