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Paper Details

Potent and uniform fetal hemoglobin induction via base editing.
Nat Genet
10
2023
Author NameAffiliation
Gregory A NewbyMerkin Institute of Transformative Technologies in Healthcare, Broad Institute of Harvard and MIT
Gregory A NewbyHoward Hughes Medical Institute, Harvard University
Gregory A NewbyHarvard University
Guolian KangSt. Jude Children's Research Hospital
Shondra M Pruett-MillerSt. Jude Children's Research Hospital
David R LiuMerkin Institute of Transformative Technologies in Healthcare, Broad Institute of Harvard and MIT
David R LiuHarvard University
David R LiuHoward Hughes Medical Institute, Harvard University
Mitchell J WeissSt. Jude Children's Research Hospital
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