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Paper Details

A Compact, High-Accuracy Cas9 with a Dinucleotide PAM for In Vivo Genome Editing.
Molecular Cell
149
2019
CRISPR, Cas9, Cas9s, Dinucleotide PAM, N4CC, Neisseria meningitidis, Nme2Cas9, PAMs, Pcsk9, cholesterol, guide RNA, mice, mouse, pre-, pre-implanted zygotes, protospacer-adjacent motifs, recognition sequences, simple dinucleotide PAM, target DNA, target site
Author NameAffiliation
Ildar GainetdinovRNA Therapeutics Institute, University of Massachusetts Medical School
Chun-Qing SongRNA Therapeutics Institute, University of Massachusetts Medical School
Yueying CaoRNA Therapeutics Institute, University of Massachusetts Medical School
Wen XueRNA Therapeutics Institute, University of Massachusetts Medical School
Erik J SontheimerRNA Therapeutics Institute, University of Massachusetts Medical School
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