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Paper Details
Paper Title
Specific Correction of Alternative Survival Motor Neuron 2 Splicing by Small Molecules: Discovery of a Potential Novel Medicine To Treat Spinal Muscular Atrophy.
PubMed
Paper Journal Title
Journal of Medicinal Chemistry
Paper Citation Count
63
Paper Publication Year
2016
Bio Mention
RG7800, SMA, SMN protein, SMN1, SMN2, SMN2 mRNA, SMN7 protein, Spinal Muscular Atrophy, Spinal muscular atrophy, Survival, Survival Motor Neuron 2, exon 7, full-length SMN protein, full-length SMN2 mRNA, human, infant, mouse, pyridopyrimidinone, survival motor neuron 1, survival motor neuron 1 (SMN1) gene, truncated
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Author Name
Affiliation
Marla Weetall
Inc.
Nikolai A Naryshkin
Inc.
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