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Paper Details

MicroRNA-regulated, systemically delivered rAAV9: a step closer to CNS-restricted transgene expression.
Mol Ther
126
2011
5' and 3' mRNA fragments, CNS disorders, MicroRNA, miRNA, miRNAs, rAAV, rAAV9, rAAV9 genome, transgene, transgene mRNA
Author NameAffiliation
Jun XieUniversity of Massachusetts Medical School
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