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Paper Title
Autophagy guided interventions to modify the cardiac phenotype of Danon disease.
PubMed
Paper Journal Title
Biochem Pharmacol
Paper Citation Count
6
Paper Publication Year
2022
Bio Mention
Cardiomyopathy, Danon, Danon disease, Danon's, Danon's cardiomyopathy, LAMP2, LAMP2 gene, LAMP2 protein, LAMP2 protein deficiency, Mice, X-linked genetic syndrome, autophagy arrest, cardiac disease, cardiac hypertrophy, cardiomyopathy, dilated cardiomyopathy, exon 6 deletion, human, humans, hydroxychloroquine, left ventricular dilatation, mice, mouse, multisystem disorder, patients, rapamycin, systolic dysfunction
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Author Name
Affiliation
Jonathan G Seidman
Harvard Medical School
Jonathan G Seidman
Harvard Medical School
Christine E Seidman
Harvard Medical School, USA Howard Hughes Medical Institute and Cardiovascular Division, Brigham and Women's Hospital
Christine E Seidman
Harvard Medical School, USA Howard Hughes Medical Institute and Cardiovascular Division, Brigham and Women's Hospital
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