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Paper Title
CRISPR interference to evaluate modifiers of <i>C9ORF72</i>-mediated toxicity in FTD.
PubMed
Paper Journal Title
Front Cell Dev Biol
Paper Citation Count
1
Paper Publication Year
2023
Bio Mention
ALS, Amyotrophic lateral sclerosis, C9, CRISPRi, Cas9, Chromosome 9 open reading frame 72, DPRs, FTD, Frontotemporal dementia, STMN2, STMN2 protein, Stmn2, TAR DNA binding protein, TDP-43, Tdp-43, dipeptide, dipeptide repeat proteins, disease-, familial FTD, mice, mouse, neurodegenerative disease, pTdp-43, single guide RNA, stathmin-2
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Author Name
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Neill R Graff-Radford
Mayo Clinic
Bradley F Boeve
Mayo Clinic
Ronald C Petersen
Mayo Clinic
Dennis W Dickson
Mayo Clinic
Dennis W Dickson
Mayo Clinic
Dennis W Dickson
Mayo Clinic
Leonard Petrucelli
Mayo Clinic
Leonard Petrucelli
Mayo Clinic
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