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Paper Details

In Vivo Repair of a Protein Underlying a Neurological Disorder by Programmable RNA Editing.
Cell Rep
36
2020
MeCP2 protein, Mecp2, Mecp2 RNA, Mecp2317G, Mecp2317G>A, Neurological Disorder, RNA 2, Rett syndrome, adenosine, adenosine deaminase, endogenous mutant RNA, guanosine, heterochromatin, hippocampal, hippocampal neuronal populations, methyl CpG binding protein 2 RNA, mice, mouse, neurodevelopmental disease, neurological disease, neuronal population, neurons, off-target editing sites, transcriptome RNA
Amino Acid Sequence, Animals, Cell Line, Gene Expression Profiling, Genetic Therapy, HEK293 Cells, Heterochromatin, Hippocampus, Humans, Male, Methyl-CpG-Binding Protein 2, Mice, Nervous System Diseases, RNA, RNA Editing, Stereotaxic Techniques
Author NameAffiliation
John R SinnamonVollum Institute, Oregon Health and Science University
Susan Y KimVollum Institute, Oregon Health and Science University
Jenna R FiskVollum Institute, Oregon Health and Science University
Zhen SongOregon Health and Science University
Hiroyuki NakaiOregon Health and Science University
Sophia JengDepartment of Medical Informatics and Clinical Epidemiology, Knight Cancer Institute, Oregon Health and Science University
Shannon K McWeeneyDepartment of Medical Informatics and Clinical Epidemiology, Knight Cancer Institute, Oregon Health and Science University
Gail MandelVollum Institute, Oregon Health and Science University
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