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Paper Details

The Clinical Outcome Study for dysferlinopathy: An international multicenter study.
Neurol Genet
65
2016
Author NameAffiliation
Avital CnaanThe John Walton Muscular Dystrophy Research Centre (E.H., Institute of Genetic Medicine, Institute for Cellular Medicine, Newcastle University, UK Jain Foundation, Inc. (L.R.), Center for Translational Science, George Washington University Department of Neurology (D.X.B.-G.), DC National Institutes of Health (NINDS) (D.X.B.-G.), MD Carolinas Healthcare System Neurosciences Institute (E.B.), Institute of Myology, Pitie-Salpetriere University Hospital, France Stanford University School of Medicine (J.W.D., Hospital de la Santa Creu i Sant Pau, Spain Muscle Research Unit (U.G., Experimental and Clinical Research Center, A Joint Cooperation of the Charite Medical Faculty and the Max Delbruck Center for Molecular Medicine, Germany Washington University (M.H., MO Institute for Neuroscience and Muscle Research (K.J.J.), Children's Hospital at Westmead, University of Sydney, Australia Nationwide Children's Hospital (J.R.M.), National Center Hospital, Hospital U. Virgen del Rocio, Instituto de Biomedicina de Sevilla, University of Padova, La Timone Hospital
Hanns Lochm??llerThe John Walton Muscular Dystrophy Research Centre (E.H., Institute of Genetic Medicine, Institute for Cellular Medicine, Newcastle University, UK Jain Foundation, Inc. (L.R.), Center for Translational Science, George Washington University Department of Neurology (D.X.B.-G.), DC National Institutes of Health (NINDS) (D.X.B.-G.), MD Carolinas Healthcare System Neurosciences Institute (E.B.), Institute of Myology, Pitie-Salpetriere University Hospital, France Stanford University School of Medicine (J.W.D., Hospital de la Santa Creu i Sant Pau, Spain Muscle Research Unit (U.G., Experimental and Clinical Research Center, A Joint Cooperation of the Charite Medical Faculty and the Max Delbruck Center for Molecular Medicine, Germany Washington University (M.H., MO Institute for Neuroscience and Muscle Research (K.J.J.), Children's Hospital at Westmead, University of Sydney, Australia Nationwide Children's Hospital (J.R.M.), National Center Hospital, Hospital U. Virgen del Rocio, Instituto de Biomedicina de Sevilla, University of Padova, La Timone Hospital
Volker StraubThe John Walton Muscular Dystrophy Research Centre (E.H., Institute of Genetic Medicine, Institute for Cellular Medicine, Newcastle University, UK Jain Foundation, Inc. (L.R.), Center for Translational Science, George Washington University Department of Neurology (D.X.B.-G.), DC National Institutes of Health (NINDS) (D.X.B.-G.), MD Carolinas Healthcare System Neurosciences Institute (E.B.), Institute of Myology, Pitie-Salpetriere University Hospital, France Stanford University School of Medicine (J.W.D., Hospital de la Santa Creu i Sant Pau, Spain Muscle Research Unit (U.G., Experimental and Clinical Research Center, A Joint Cooperation of the Charite Medical Faculty and the Max Delbruck Center for Molecular Medicine, Germany Washington University (M.H., MO Institute for Neuroscience and Muscle Research (K.J.J.), Children's Hospital at Westmead, University of Sydney, Australia Nationwide Children's Hospital (J.R.M.), National Center Hospital, Hospital U. Virgen del Rocio, Instituto de Biomedicina de Sevilla, University of Padova, La Timone Hospital
Kate BushbyThe John Walton Muscular Dystrophy Research Centre (E.H., Institute of Genetic Medicine, Institute for Cellular Medicine, Newcastle University, UK Jain Foundation, Inc. (L.R.), Center for Translational Science, George Washington University Department of Neurology (D.X.B.-G.), DC National Institutes of Health (NINDS) (D.X.B.-G.), MD Carolinas Healthcare System Neurosciences Institute (E.B.), Institute of Myology, Pitie-Salpetriere University Hospital, France Stanford University School of Medicine (J.W.D., Hospital de la Santa Creu i Sant Pau, Spain Muscle Research Unit (U.G., Experimental and Clinical Research Center, A Joint Cooperation of the Charite Medical Faculty and the Max Delbruck Center for Molecular Medicine, Germany Washington University (M.H., MO Institute for Neuroscience and Muscle Research (K.J.J.), Children's Hospital at Westmead, University of Sydney, Australia Nationwide Children's Hospital (J.R.M.), National Center Hospital, Hospital U. Virgen del Rocio, Instituto de Biomedicina de Sevilla, University of Padova, La Timone Hospital
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