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Paper Details

Inhaled gene therapy of preclinical muco-obstructive lung diseases by nanoparticles capable of breaching the airway mucus barrier.
Thorax
6
2022
ENaC, ENaC-silencing plasmids, MPP, Scnn1b, Scnn1b-Tg, cystic fibrosis, epithelial sodium channel, human, human bronchial epithelial cells, mice, mouse, muco-obstructive lung diseases, mucus stasis, plasmid, primary, rare gene, reporter transgene, synthetic DNA, transgene
Author NameAffiliation
Richard C BoucherMarisco Lung Institute and Cystic Fibrosis Research Center, University of North Carolina School of Medicine
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