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Paper Title
Pharmacological reversal of synaptic and network pathology in human MECP2-KO neurons and cortical organoids.
PubMed
Paper Journal Title
EMBO Mol Med
Paper Citation Count
44
Paper Publication Year
2021
Bio Mention
MECP2, MECP2 mutations, MECP2-mosaic neurospheres, MeCP2, MeCP2 deficiency, Nefiracetam, PHA 543613, RTT, Rett syndrome, X-linked MECP2 gene, cortical organoids, human, human MECP2-KO neurons, human neurons, human pluripotent stem cell, neurodevelopmental disorders, neurodevelopmental impairment
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Author Name
Affiliation
Cleber A Trujillo
Department of Pediatrics/Rady Children's Hospital, University of California San Diego
Priscilla D Negraes
Department of Pediatrics/Rady Children's Hospital, University of California San Diego
Priscilla D Negraes
Terrence J Sejnowski
Salk Institute for Biological Studies
Terrence J Sejnowski
University of California San Diego
Terrence J Sejnowski
Institute for Neural Computation, University of California San Diego
Alysson R Muotri
Department of Pediatrics/Rady Children's Hospital, University of California San Diego
Alysson R Muotri
Center for Academic Research and Training in Anthropogeny, University of California San Diego
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