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Paper Details

Lentivirus-mediated gene therapy for Fabry disease.
Nat Commun
47
2021
-gal A, CD34+, CD34+-selected,, CD34+-selected, hematopoietic stem/progenitor cells, Fabry disease, Gb3, alpha-galactosidase A, bone marrow cells, globotriaosylsphingosine (lyso-Gb3), hematopoietic stem/progenitor cells, leukocytes, melphalan, patient, patients, peripheral blood, transduced,, urine globotriaosylceramide
Author NameAffiliation
Daniel H Fowler
Daniel H Fowler
Jeffrey A MedinUniversity Health Network
Jeffrey A MedinMedical College of Wisconsin
Jeffrey A MedinMedical College of Wisconsin
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