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Paper Details

In vivo base editing rescues cone photoreceptors in a mouse model of early-onset inherited retinal degeneration.
Nat Commun
35
2022
ABE, ABEs, LCA, Leber congenital amaurosis, RPE65, Rpe65, Rpe65 transcripts, adenine, children, cone, cone photoreceptor, cone photoreceptors, cones, genes, inherited retinal degeneration, mice, mouse, patients, photoreceptors, sgRNA, sgRNAs, visual impairment
Author NameAffiliation
Gregory A NewbyMerkin Institute of Transformative Technologies in Healthcare at Broad Institute
Gregory A NewbyHoward Hughes Medical Institute, Harvard University
Gregory A NewbyHarvard University
Seth BlackshawJohns Hopkins University School of Medicine
David R LiuMerkin Institute of Transformative Technologies in Healthcare at Broad Institute
David R LiuHarvard University
David R LiuHoward Hughes Medical Institute, Harvard University
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