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Paper Details

Prednisolone rescues Duchenne muscular dystrophy phenotypes in human pluripotent stem cell-derived skeletal muscle in vitro.
Proc Natl Acad Sci U S A
31
2021
DMD, DMD iPSC lines, DMD-mutant iPSC lines, Duchenne muscular dystrophy, Prednisolone, calcium, degeneration of skeletal muscles, dystrophin, dystrophin-associated glycoprotein complex, genetic disease, human, human induced pluripotent stem cells, human pluripotent stem, human pluripotent stem cell-derived skeletal muscle, iPSC, isogenic, muscle wasting, myofiber, myofibers, myogenic cultures, prednisolone, premature death
Author NameAffiliation
Bianca HabermannAix-Marseille University, CNRS, Institut de Biologie du Developpement de Marseille UMR 7288, The Turing Center for Living Systems
Bianca HabermannAix-Marseille University, CNRS, Institut de Biologie du Developpement de Marseille UMR 7288, The Turing Center for Living Systems
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