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Paper Title
Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction.
PubMed
Paper Journal Title
Cell Res
Paper Citation Count
44
Paper Publication Year
2019
Bio Mention
cell types, dominant point mutation, genetic disease, homology arm donor, inherited diseases, intracellularly linearized single homology arm donor, intron, minigene, mouse, premature-aging, target gene locus
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Author Name
Affiliation
Pierre J Magistretti
King Abdullah University of Science and Technology (KAUST)
Carlos L??pez-Ot??n
Instituto Universitario de Oncologia (IUOPA), Universidad de Oviedo
Kun Zhang
University of California
Kun Zhang
University of California
Juan Carlos Izpisua Belmonte
Salk Institute for Biological Studies
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