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Paper Details

Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction.
Cell Res
44
2019
cell types, dominant point mutation, genetic disease, homology arm donor, inherited diseases, intracellularly linearized single homology arm donor, intron, minigene, mouse, premature-aging, target gene locus
Author NameAffiliation
Pierre J MagistrettiKing Abdullah University of Science and Technology (KAUST)
Carlos L??pez-Ot??nInstituto Universitario de Oncologia (IUOPA), Universidad de Oviedo
Kun ZhangUniversity of California
Kun ZhangUniversity of California
Juan Carlos Izpisua BelmonteSalk Institute for Biological Studies
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