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Paper Details

2-Year Change in Revised Hammersmith Scale Scores in a Large Cohort of Untreated Paediatric Type 2 and 3 SMA Participants.
J Clin Med
2
2023
Atrophy, Participants, RHS, RULM, SMA, SMA 2 and 3, Spinal Muscular, Type 2 and 3 SMA, participant, participants, patients
Author NameAffiliation
Enrico BertiniBambino Gesu Children's Hospital, IRCCS
Enrico BertiniBambino Gesu Children's Hospital, IRCCS
Basil T DarrasBoston Children's Hospital, Harvard Medical School
Richard S FinkelNemours Children's Hospital and University of Central Florida College of Medicine
Richard S FinkelSt. Jude Children's Research Hospital
Francesco MuntoniUniversity of Suffolk
Francesco MuntoniNational Institute for Health Research Great Ormond Street Hospital Biomedical Research Centre
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