| Robert J Graham | Boston Children's Hospital, Harvard Medical School |
| Francesco Muntoni | UCL Great Ormond Street Institute of Child Health and NIHR Great Ormond Street Hospital Biomedical Research Centre |
| Nancy L Kuntz | Ann and Robert H Lurie Children's Hospital of Chicago |
| Casie A Genetti | The Manton Center for Orphan Disease Research, Boston Children's Hospital, Harvard Medical School |
| Alan H Beggs | The Manton Center for Orphan Disease Research, Boston Children's Hospital, Harvard Medical School |