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Paper Details

Mortality and respiratory support in X-linked myotubular myopathy: a RECENSUS retrospective analysis.
Arch Dis Child
23
2020
Author NameAffiliation
Robert J GrahamBoston Children's Hospital, Harvard Medical School
Francesco MuntoniUCL Great Ormond Street Institute of Child Health and NIHR Great Ormond Street Hospital Biomedical Research Centre
Nancy L KuntzAnn and Robert H Lurie Children's Hospital of Chicago
Casie A GenettiThe Manton Center for Orphan Disease Research, Boston Children's Hospital, Harvard Medical School
Alan H BeggsThe Manton Center for Orphan Disease Research, Boston Children's Hospital, Harvard Medical School
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