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Paper Details

Short-Term Administration of Mycophenolate Is Well-Tolerated in CLN3 Disease (Juvenile Neuronal Ceroid Lipofuscinosis).
JIMD Rep
23
2019
CLN3, CLN3 Disease, CLN3 disease, Juvenile Neuronal Ceroid Lipofuscinosis, Mycophenolate, autoimmune neurological conditions, diarrhea, inflammation, mycophenolate, neurodegenerative disorder, participants, vomiting
Author NameAffiliation
Erika F AugustineUniversity of Rochester Medical Center
Erika F AugustineUniversity of Rochester Medical Center
Erika F AugustineCenter for Health + Technology, University of Rochester Medical Center
Jill M Weimer
Jonathan W MinkUniversity of Rochester Medical Center
Jonathan W MinkUniversity of Rochester Medical Center
Jonathan W MinkUniversity of Rochester Medical Center
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