Skip to Main Content

Paper Details

Use of funded multicenter prospective longitudinal databases to inform clinical trials in rare diseases-Examination of cholestatic liver disease in Alagille syndrome.
Hepatol Commun
4
2022
ALGS, Alagille Syndrome, Alagille syndrome, ITCH, alanine, alanine aminotransferase, albumin, bile acid, bilirubin, children, cholestasis, cholestatic liver disease, maralixibat, orphan diseases, participants, platelet, pruritus, rare
Author NameAffiliation
Cathie SpinoUniversity of MichiganAnn ArborMichiganUSA.
Estella M Alonsoand NutritionAnn & Robert H. Lurie Children's Hospital of ChicagoNorthwestern University Feinberg School of MedicineChicagoIllinoisUSA.
Simon HorslenDepartment of PediatricsSeattle Children's HospitalUniversity of Washington School of MedicineSeattleWAUSA.
Philip J RosenthalDepartment of PediatricsUniversity of California san francisco
Robert H Squiresand NutritionDepartment of PediatricsUniversity of PittsburghSchool of Medicine and Children's Hospital of Pittsburgh of University of Pittsburgh Medical CenterPittsburghPennsylvaniaUSA.
Robert H Squiresand NutritionDepartment of PediatricsUniversity of PittsburghSchool of Medicine and Children's Hospital of Pittsburgh of University of Pittsburgh Medical CenterPittsburghPennsylvaniaUSA.
Ronald J SokolHepatology and NutritionUniversity of Colorado School of Medicine and Children's Hospital ColoradoAuroraColoradoUSA.
  • 1 - 7

Datasets

Release 1.2