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Paper Details

Response of plasma microRNAs to nusinersen treatment in patients with SMA.
Ann Clin Transl Neurol
4
2022
Author NameAffiliation
Francesco MuntoniGreat Ormond Street Institute of Child Health, University College London
Francesco MuntoniGreat Ormond Street Hospital
Francesco MuntoniNIHR Great Ormond Street Hospital Biomedical Research Centre
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