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Paper Details
Paper Title
Nusinersen in pediatric and adult patients with type III spinal muscular atrophy.
PubMed
Paper Journal Title
Ann Clin Transl Neurol
Paper Citation Count
23
Paper Publication Year
2021
Bio Mention
HFMSE, Patients, SMN2, patients, pediatric, type III, type III SMA, type III spinal muscular atrophy
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Author Name
Affiliation
Basil T Darras
Boston Children's Hospital, Harvard Medical School
Enrico Bertini
IRCCS Bambino Gesu Children's Hospital
Enrico Bertini
IRCCS Bambino Gesu Children's Hospital
Francesco Muntoni
UCL Institute of Child Health & Great Ormond Street Hospital
Francesco Muntoni
NIHR Great Ormond Street Hospital Biomedical Research Centre
Richard S Finkel
Nemours Children's Hospital, University of Central Florida College of Medicine
Richard S Finkel
St. Jude Children's Research Hospital
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