Skip to Main Content

Paper Details

Nusinersen in pediatric and adult patients with type III spinal muscular atrophy.
Ann Clin Transl Neurol
23
2021
HFMSE, Patients, SMN2, patients, pediatric, type III, type III SMA, type III spinal muscular atrophy
Author NameAffiliation
Basil T DarrasBoston Children's Hospital, Harvard Medical School
Enrico BertiniIRCCS Bambino Gesu Children's Hospital
Enrico BertiniIRCCS Bambino Gesu Children's Hospital
Francesco MuntoniUCL Institute of Child Health & Great Ormond Street Hospital
Francesco MuntoniNIHR Great Ormond Street Hospital Biomedical Research Centre
Richard S FinkelNemours Children's Hospital, University of Central Florida College of Medicine
Richard S FinkelSt. Jude Children's Research Hospital
  • 1 - 7

Datasets