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Paper Details

Lentiviral gene therapy and vitamin B3 treatment enable granulocytic differentiation of G6PC3-deficient induced pluripotent stem cells.
Gene Ther
6
2020
Author NameAffiliation
Doris SteinemannInstitute of Cell and Molecular Pathology, Hannover Medical School
Christoph KleinDr. von Hauner Children's Hospital University Hospital, Ludwig-Maximilians-University Munich
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