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Paper Details

Applying genome-wide CRISPR-Cas9 screens for therapeutic discovery in facioscapulohumeral muscular dystrophy.
Sci Transl Med
41
2020
CRISPR, Cas9, DUX4, DUX4 protein, FSHD, FSHD disease, cell, facioscapulohumeral muscular dystrophy, genetic disease, genetic disorders, muscle cells, muscular dystrophy, patient myogenic lines, zebrafish
Author NameAffiliation
Andrew KodaniBoston Children's Hospital
Andrew KodaniHarvard Medical School
Monkol LekYale School of Medicine
Louis M KunkelBoston Children's Hospital
Louis M KunkelHarvard Medical School
Louis M KunkelHarvard Stem Cell Institute
Louis M KunkelManton Center for Orphan Disease Research, Boston Children's Hospital, Harvard Medical School
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Release 1.2