|
| 36719755 | DG9-conjugated morpholino rescues phenotype in SMA mice by reaching the CNS via a subcutaneous administration. | JCI Insight | 2023 |
| 34808387 | Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model. | Mol Ther | 2022 |
| 36197970 | Common and species-specific molecular signatures, networks, and regulators of influenza virus infection in mice, ferrets, and humans. | Sci Adv | 2022 |
| 35263596 | The RNA helicase DHX16 recognizes specific viral RNA to trigger RIG-I-dependent innate antiviral immunity. | Cell Rep | 2022 |
| 35193974 | Development of DG9 peptide-conjugated single- and multi-exon skipping therapies for the treatment of Duchenne muscular dystrophy. | Proc Natl Acad Sci U S A | 2022 |
| 33164048 | Inhibition of SARS-CoV-2 in Vero cell cultures by peptide-conjugated morpholino oligomers. | J Antimicrob Chemother | 2021 |
| 34884867 | A <i>Dystrophin</i> Exon-52 Deleted Miniature Pig Model of Duchenne Muscular Dystrophy and Evaluation of Exon Skipping. | Int J Mol Sci | 2021 |
| 34556855 | Restriction factor compendium for influenza A virus reveals a mechanism for evasion of autophagy. | Nat Microbiol | 2021 |
| 34107015 | Enhanced delivery of peptide-morpholino oligonucleotides with a small molecule to correct splicing defects in the lung. | Nucleic Acids Res | 2021 |
| 34037420 | CX3CR1 Is a Receptor for Human Respiratory Syncytial Virus in Cotton Rats. | J Virol | 2021 |
| 34319155 | Hemagglutinins of Avian Influenza Viruses Are Proteolytically Activated by TMPRSS2 in Human and Murine Airway Cells. | J Virol | 2021 |
| 33337582 | MOTS-c promotes phosphorodiamidate morpholino oligomer uptake and efficacy in dystrophic mice. | EMBO Mol Med | 2021 |
| 32703818 | TMPRSS2 and furin are both essential for proteolytic activation of SARS-CoV-2 in human airway cells. | Life Sci Alliance | 2020 |
| 33024974 | Inhibition of SARS-CoV-2 in Vero cell cultures by peptide-conjugated morpholino-oligomers. | bioRxiv | 2020 |
| 33294290 | Erratum: Fructose Promotes Uptake and Activity of Oligonucleotides with Different Chemistries in a Context-Dependent Manner in <i>mdx</i> Mice. | Mol Ther Nucleic Acids | 2020 |
| 32920261 | Context Dependent Effects of Chimeric Peptide Morpholino Conjugates Contribute to Dystrophin Exon-skipping Efficiency. | Mol Ther Nucleic Acids | 2020 |
| 32888402 | Functional Rescue of Dystrophin-Deficient mdx Mice by a Chimeric Peptide-PMO. | Mol Ther | 2020 |
| 32888401 | Effective Dystrophin Restoration by a Novel Muscle-Homing Peptide-Morpholino Conjugate in Dystrophin-Deficient mdx Mice. | Mol Ther | 2020 |
| 30428047 | A fusion peptide directs enhanced systemic dystrophin exon skipping and functional restoration in dystrophin-deficient mdx mice. | Hum Mol Genet | 2019 |
| 31682641 | The ETS transcription factor ELF1 regulates a broadly antiviral program distinct from the type I interferon response. | PLoS Pathog | 2019 |
| 31629961 | Hexose Potentiates Peptide-Conjugated Morpholino Oligomer Efficacy in Cardiac Muscles of Dystrophic Mice in an Age-Dependent Manner. | Mol Ther Nucleic Acids | 2019 |
| 31391268 | TMPRSS2 Is the Major Activating Protease of Influenza A Virus in Primary Human Airway Cells and Influenza B Virus in Human Type II Pneumocytes. | J Virol | 2019 |
| 30345257 | CSGID Solves Structures and Identifies Phenotypes for Five Enzymes in <i>Toxoplasma gondii</i>. | Front Cell Infect Microbiol | 2018 |
| 29875202 | Anchor peptide captures, targets, and loads exosomes of diverse origins for diagnostics and therapy. | Sci Transl Med | 2018 |
| 30171549 | A Novel Zebrafish Model for Assessing In Vivo Delivery of Morpholino Oligomers. | Methods Mol Biol | 2018 |
| 28373570 | Effects of systemic multiexon skipping with peptide-conjugated morpholinos in the heart of a dog model of Duchenne muscular dystrophy. | Proc Natl Acad Sci U S A | 2017 |
| 28364249 | Surface Plasmon Resonance-Based Concentration Determination Assay: Label-Free and Antibody-Free Quantification of Morpholinos. | Methods Mol Biol | 2017 |
| 28364231 | Aggregation and Disaggregation of Morpholino Oligomers in Solution. | Methods Mol Biol | 2017 |
| 28248290 | Systems-based analysis of RIG-I-dependent signalling identifies KHSRP as an inhibitor of RIG-I receptor activation. | Nat Microbiol | 2017 |
| 27412848 | New paradigms for understanding and step changes in treating active and chronic, persistent apicomplexan infections. | Sci Rep | 2016 |
| 27351681 | Fructose Promotes Uptake and Activity of Oligonucleotides With Different Chemistries in a Context-dependent Manner in mdx Mice. | Mol Ther Nucleic Acids | 2016 |
| 25951508 | The zebrafish, Danio rerio, as a model for Toxoplasma gondii: an initial description of infection in fish. | J Fish Dis | 2015 |
| 26651948 | Meta- and Orthogonal Integration of Influenza "OMICs" Data Defines a Role for UBR4 in Virus Budding. | Cell Host Microbe | 2015 |
| 24636820 | Effect of combined systemic and local morpholino treatment on the spinal muscular atrophy ο7 mouse model phenotype. | Clin Ther | 2014 |
| 24732757 | Effective dystrophin restoration by a novel muscle-homing peptide-morpholino conjugate in dystrophin-deficient mdx mice. | Mol Ther | 2014 |
| 24942628 | Exon skipping restores dystrophin expression, but fails to prevent disease progression in later stage dystrophic dko mice. | Gene Ther | 2014 |
| 24882218 | Unanchored K48-linked polyubiquitin synthesized by the E3-ubiquitin ligase TRIM6 stimulates the interferon-IKKε kinase-mediated antiviral response. | Immunity | 2014 |
| 23140456 | In vivo delivery of morpholino oligos by cell-penetrating peptides. | Curr Pharm Des | 2013 |
| 24064708 | Context Dependent Effects of Chimeric Peptide Morpholino Conjugates Contribute to Dystrophin Exon-skipping Efficiency. | Mol Ther Nucleic Acids | 2013 |
| 22683468 | Long-term rescue of dystrophin expression and improvement in muscle pathology and function in dystrophic mdx mice by peptide-conjugated morpholino. | Am J Pathol | 2012 |
| 22454076 | Cell-penetrating peptides enhance systemic delivery of antisense morpholino oligomers. | Methods Mol Biol | 2012 |
| 21062902 | Diaphragm rescue alone prevents heart dysfunction in dystrophic mice. | Hum Mol Genet | 2011 |
| 21825302 | Development of peptide-conjugated morpholino oligomers as pan-arenavirus inhibitors. | Antimicrob Agents Chemother | 2011 |
| 21053140 | CPP-directed oligonucleotide exon skipping in animal models of Duchenne muscular dystrophy. | Methods Mol Biol | 2011 |
| 19815563 | Long-term improvement in mdx cardiomyopathy after therapy with peptide-conjugated morpholino oligomers. | Cardiovasc Res | 2010 |
| 20700113 | Functional rescue of dystrophin-deficient mdx mice by a chimeric peptide-PMO. | Mol Ther | 2010 |
| 20170628 | Morpholinos and their peptide conjugates: therapeutic promise and challenge for Duchenne muscular dystrophy. | Biochim Biophys Acta | 2010 |
| 20332768 | Dystrophin isoform induction in vivo by antisense-mediated alternative splicing. | Mol Ther | 2010 |
| 20235089 | In vitro evaluation of novel antisense oligonucleotides is predictive of in vivo exon skipping activity for Duchenne muscular dystrophy. | J Gene Med | 2010 |
| 19223614 | Chemical modifications of antisense morpholino oligomers enhance their efficacy against Ebola virus infection. | Antimicrob Agents Chemother | 2009 |