Author details

Full Name

Terence R Flotte

Affiliation

ORCID

Career Start Year

1988

Papers

301

H Index

Expertise

CM4AI Collaborator

PMID	Paper Title	Journal Title	Published Year
36728995	Defining Scholarship for Today and Tomorrow.		2023
36825473	Gene therapy for alpha-1 antitrypsin deficiency: an update.		2023
36862289	Immunogenicity of Recombinant Adeno-Associated Virus (AAV) Vectors for Gene Transfer.		2023
36794978	Future Directions and Resource Needs for National Heart, Lung, and Blood Institute (NHLBI) Gene Therapy Research: A Report of an NHLBI Workshop.	Hum Gene Ther	2023
36924775	Analyzing clinical observations to better understand and manage immune responses to AAV gene therapies.		2023
35102556	Gene Therapy for Rare Neurological Disorders.	Clinical Pharmacology and Therapeutics	2022
35592360	Liver-directed gene therapy attenuates progression of spontaneous and tobacco smoke-induced emphysema in Î±1-antitrypsin null mice.	Molecular Therapy - Methods and Clinical Development	2022
35972326	Gene Therapy for Endocrine Disorders: A Promising Intervention.	Human Gene Therapy	2022
35585789	Gene-based therapeutics for rare genetic neurodevelopmental psychiatric disorders.	Mol Ther	2022
35901208	Secretion of functional Î±1-antitrypsin is cell type dependent: Implications for intramuscular delivery for gene therapy.	Proceedings of the National Academy of Sciences of the United States of America	2022
35576406	Gene Therapy and the Use of Animal Models: Why Mice Alone Are Not Sufficient.	Human Gene Therapy	2022
36125440	ESGCT 2022: The New Normal for the Gene Therapy Community.	Human Gene Therapy	2022
35145305	AAV gene therapy for Tay-Sachs disease.	Nat Med	2022
34433081	InÂ vivo gene editing works in humans: Results of a phase 1 clinical trial for TTR amyloidosis.	Molecular Therapy	2021
33750221	CRISPR/Cas-Dependent and Nuclease-Free Therapeutic Gene Editing.	Human Gene Therapy	2021
33750218	CRISPR Keeps Things Fresh: Next-Generation Tools for Gene Editing.	Human Gene Therapy	2021
34283641	Base Editing to the Rescue.	Human Gene Therapy	2021
34283643	Immune Responses to Recombinant Adenoviruses As Gene Therapy Vectors and COVID-19 Vaccines: A Two-Edged Sword.	Human Gene Therapy	2021
33471605	Gene and Cell Therapy for Inherited and Acquired Immune Deficiency.	Human Gene Therapy	2021
34003043	Gene Therapy in Global Health: Meeting the Needs of Chinese Patients with Beta-Thalassemia.	Human Gene Therapy	2021
34003044	It Is Time to Call Anti-Asian Bias What It Is: Racism.	Human Gene Therapy	2021
33891503	Women Lead Gene Therapy Science in 2021.	Human Gene Therapy	2021
33782545	Large-scale molecular epidemiological analysis of AAV in a cancer patient population.	Oncogene	2021
33570854	In Reply to Ramotshwana et al.	Academic Medicine	2021
33837189	Improved prime editors enable pathogenic allele correction and cancer modelling in adult mice.	Nature Communications	2021
33765033	Common pathways to Dean of Medicine at U.S. medical schools.	PLoS One	2021
33863844	Supporting Families Considering Participation in a Clinical Trial: Parent-Provider Perspectives.	Pediatrics	2021
33547423	Liver targeting with rAAV7: balancing tropism with immune profiles.	Gene Therapy	2021
34780289	Precision of Exon Skipping with U7 Constructs.	Human Gene Therapy	2021
34662234	ESGCT 2021: Virtually Pan-European.	Human Gene Therapy	2021
32605399	Moving Forward After Two Deaths in a Gene Therapy Trial of Myotubular Myopathy.	Human Gene Therapy	2020
32202458	Impact on Women's Health: Gene Therapy in Gynecologic Oncology.	Human Gene Therapy	2020
31967921	2020: Gene Therapy Enters Its Fourth Decade.	Human Gene Therapy	2020
31967920	Gene Therapy Untangles the Problem of Chronic Traumatic Encephalopathy.	Human Gene Therapy	2020
31967918	Ringing in the Changes.	Human Gene Therapy	2020
32073927	Free Gene and Cell Therapy Services Offered by the National Heart, Lung, and Blood Institute of the National Institutes of Health.	Human Gene Therapy	2020
32363942	Volume and Infusion Rate Dynamics of Intraparenchymal Central Nervous System Infusion in a Large Animal Model.	Human Gene Therapy	2020
32302233	Revisiting the "New" Inflammatory Toxicities of Adeno-Associated Virus Vectors.	Human Gene Therapy	2020
31625994	Women's Representation Among Members and Leaders of National Medical Specialty Societies.	Academic Medicine	2020
32212981	A Message to Our Community in the Midst of the COVID-19 Pandemic.	Human Gene Therapy	2020
31982038	Muscle-Directed Delivery of an AAV1 Vector Leads to Capsid-Specific T Cell Exhaustion in Nonhuman Primates and Humans.	Molecular Therapy	2020
31813800	A Safe and Reliable Technique for CNS Delivery of AAV Vectors in the Cisterna Magna.	Molecular Therapy	2020
32384022	Barrie J. Carter: The Science and the Scientist.	Human Gene Therapy	2020
31860618	In Reply to Signer and Curtin and to Goyal et al.	Academic Medicine	2020
32520751	Accelerated Graduation and the Deployment of New Physicians During the COVID-19 Pandemic.	Academic Medicine	2020
33337270	Writing the Story of Gene Editing and CRISPR: An Interview with Kevin Davies, PhD.	Human Gene Therapy	2020
33337269	Science Policy and Funding Implications of the 2020 U.S. Election.	Human Gene Therapy	2020
33117614	Two-Plasmid Packaging System for Recombinant Adeno-Associated Virus.		2020
32607885	Engraftment of Human Hepatocytes in the PiZ-NSG Mouse Model.	Methods in Molecular Biology	2020
32716736	Black Lives Matter to Gene Therapy.	Human Gene Therapy	2020