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| 37461560 | Dual targeting of hepatocyte DGAT2 and stellate cell FASN alleviates nonalcoholic steatohepatitis in mice. | bioRxiv | 2023 |
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| 37205462 | Lactate transporter MCT1 in hepatic stellate cells promotes fibrotic collagen expression in nonalcoholic steatohepatitis. | bioRxiv | 2023 |
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| 35847173 | Chemical optimization of siRNA for safe and efficient silencing of placental sFLT1. | Mol Ther Nucleic Acids | 2022 |
| 35477658 | RNAi-based modulation of IFN-γ signaling in skin. | Mol Ther | 2022 |
| 35581683 | Delivering siRNA Compounds During HOPE to Modulate Organ Function: A Proof-of-concept Study in a Rat Liver Transplant Model. | Transplantation | 2022 |
| 35795486 | PK-modifying anchors significantly alter clearance kinetics, tissue distribution, and efficacy of therapeutics siRNAs. | Mol Ther Nucleic Acids | 2022 |
| 35688130 | Modulation of DNA transcription: The future of ASO therapeutics? | Cell | 2022 |
| 36458209 | Mutant huntingtin messenger RNA forms neuronal nuclear clusters in rodent and human brains. | Brain Commun | 2022 |
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| 35920332 | Intratracheally administered LNA gapmer antisense oligonucleotides induce robust gene silencing in mouse lung fibroblasts. | Nucleic Acids Res | 2022 |
| 35917865 | Engineered ionizable lipid siRNA conjugates enhance endosomal escape but induce toxicity in vivo. | J Control Release | 2022 |
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| 34935646 | Comparative route of administration studies using therapeutic siRNAs show widespread gene modulation in Dorset sheep. | JCI Insight | 2021 |
| 34417184 | Gene therapy with AR isoform 2 rescues spinal and bulbar muscular atrophy phenotype by modulating AR transcriptional activity. | Sci Adv | 2021 |
| 34325468 | AIM2 regulates anti-tumor immunity and is a viable therapeutic target for melanoma. | J Exp Med | 2021 |
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| 31666200 | Enriched chitosan nanoparticles loaded with siRNA are effective in lowering Huntington's disease gene expression following intranasal administration. | Nanomedicine | 2020 |
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